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Orchard Therapeutics Limited

http://orchard-tx.com/

Latest From Orchard Therapeutics Limited

Orchard To Work On Reversing English Funding Refusal For Libmeldy Gene Therapy

Health technology assessment body NICE has welcomed further discussion between Orchard Therapeutics and the National Health Service to resolve its concerns over the company’s one-time gene therapy for the neurodegenerative disorder, metachromatic leukodystrophy, in children.

Neurology Cost Effectiveness

Pharming And Orchard Seek Stem Cell Solution To Hereditary Angioedema

Orchard Therapeutics of the US and Dutch biotech Pharming have agreed to jointly research, develop, manufacture and commercialize the former’s newly disclosed investigational ex vivo autologous hematopoietic stem cell gene therapy as a treatment for hereditary angioedema.

Deals Clinical Trials

Product Accepted Twice On PRIME Marks A First For EMA

Vertex and CRISPR can now get access to the advantages afforded by the European Medicines Agency’s priority medicines scheme for both of the indications they are targeting with their investigational gene therapy, CTX001.

Regulation Europe

Alexion Deal Adds Up For AstraZeneca's Rare Disease Specialist CFO

The proposed $39bn acquisition of Alexion by AstraZeneca has a particular interest for its chief financial officer Marc Dunoyer who recently spoke to Scrip about his extensive experience in the rare disease space.

M & A Rare Diseases
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Company Information

  • Industry
  • Pharmaceuticals
  • Pharmaceuticals
    • Drug Delivery
  • Biotechnology
    • Gene Therapy, Cell Therapy
  • Other Names / Subsidiaries
    • Orchard Therapeutics (Europe) Limited, Orchard Therapeutics North America
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