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Vertex’s Price Tag For Taking More Control Of CRISPR-Partnered Candidate: At Least $900m

Change To Partnership Comes After First Positive Pivotal Data For Blood Disorders

Executive Summary

Vertex and partner CRISPR Therapeutics hope CDX001 can offer a single-use curative regimen for sickle cell disease and beta thalassemia patients. A regulatory filing is possible within 18-24 months.

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