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New CRISPR Therapeutics/Vertex Data Dangle The Hope Of Cure For SCD and TDT

Executive Summary

With more data reported at ASH, Vertex and CRISPR Therapeutics added heft to the notion that functional cures are on the horizon for the inherited blood disorders sickle cell disease and beta-thalassemia. Attention is now turning to Bluebird’s marketing strategy after a filing delay.

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