Sarepta Winning Payer War Over Duchenne Muscular Dystrophy Drug Coverage
Executive Summary
Exondys 51 has been met with recommendations for restrictions by many insurers, but after consultations with experts and Sarepta execs coverage is expanding.
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Launching much faster than it told a US FDA advisory committee that it would, Sarepta is focusing on Duchenne muscular dystrophy patients about to turn six in the initial roll-out of its gene therapy Elevidys amid fears the wait for payer authorization could mean losing access to the treatment.
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Unpredictable DMD Progression Complicates Sarepta’s Gene Therapy Efficacy Claims
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