Gene Editing: Rewriting The Code
This article was originally published in Start Up
Executive Summary
Gene editing technologies, which enable knockout or modification of specific genes, could get first use in modifying T cells to fight cancer and HIV, but its long-term potential to control gene expression in vivo has sparked Series A financings of three start-ups in the past 18 months.
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Homology Medicines Inc.
Gene editing has made a great many headlines of late, and one could be forgiven for thinking the field was saturated, but Homology Medicines Inc. offers something new. Its platform relies on a different mechanism, known as homologous recombination, and the start-up's management team believes the approach can get around some of the potential limitations found in other gene-editing technologies.