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Latest From Genethon

Audentes Set To Resume XLMTM Trial As US Hold Lifts

Trial of high-need gene therapy set to restart following the deaths of several participants and the lifting of a clinical hold imposed by the US FDA last year.

Gene Therapy Clinical Trials

Audentes' Gene Therapy Allows Ventilator Independence For Rare Disease

Audentes Therapeutics is aiming for regulatory submissions next year for its lead product, a skeletal muscle-targeted gene therapy, which continues to show promise in X-linked myotubular myopathy.

Rare Diseases Gene Therapy

Durability Seen With Novartis, Roche SMA Therapies Heading For Market

Novartis and Roche have announced additional interim clinical data as their candidate spinal muscular atrophy therapies near the marketplace.

Gene Therapy Neurology

Tech Transfer Roundup: Vanderbilt Teams With Deerfield; Expands Cancer Pact With Boehringer

Vanderbilt launches new biotech with Deerfield aimed at reworking the drug development paradigm, while also expanding its cancer research work with BI. Grunenthal partners with Katholieke Universiteit Leuven to investigate ion channel modulation approaches in pain.

Research & Development Deals
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