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uniQure N.V.

http://www.uniqure.com

Latest From uniQure N.V.

UniQure Expects To Resolve FDA Clinical Hold Within Three Months

The gene therapy EtranaDez for hemophilia B placed on clinical hold after a patient was diagnosed with liver cancer, but UniQure points to that patient’s extensive history of liver disease.

Gene Therapy Clinical Trials

Freeline Hemophilia B Gene Therapy May Have Advantage Over Competitors

UniQure has a potential first-mover advantage, but Freeline study's investigator compares FLT180a to later model smartphones with bugs fixed.

BioPharmaceutical Blood & Coagulation Disorders

Signs Of Long-Term Efficacy Boost UniQure’s Hem B Gene Therapy

Unveiling its latest data, UniQure is tipped to avoid the knockback which affected BioMarin’s hemophilia A gene therapy, with a filing expected in the second half of 2021.

BioPharmaceutical Commercial

ASH Data Bring UniQure Closer To Filing Hemophilia B Gene Therapy

The company plans to file with 52-week data for AMT-061 and is confident it won't face the same stringent requirements from the FDA that led to a complete response letter for BioMarin's Roctavian.

BioPharmaceutical Blood & Coagulation Disorders
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Company Information

  • Industry
  • Pharmaceuticals
    • Drug Delivery
  • Biotechnology
    • Antisense, Oligonucleotides
    • Gene Therapy, Cell Therapy
    • Large Molecule
  • Other Names / Subsidiaries
    • Amsterdam Molecular Therapeutics (AMT)
    • InoCard GmbH
    • uniQure Germany GmbH
    • uniQure U.S.A.
    • uniQure The Netherlands
    • uniQure Inc.
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