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With Duchenne Filing Due, Santhera Moves Vamorolone Into Becker Muscular Dystrophy

Rare Disease Trial Receiving FDA Funding

Executive Summary

Santhera is bouncing back after a Duchenne drug failure two years ago with idebenone, and is looking to gain approval of vamorolone in this indication as well as the much rarer Becker muscular dystrophy.

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Santhera's Transformation Should Turn Investors' Heads

The Swiss biotech had a tough time after the failure of idebenone for Duchenne muscular dystrophy, but CEO Dario Eklund tells Scrip that with a new soon-to-be submitted compound, vamorolone, it has an effective and much safer alternative to steroids for the treatment of the progressive muscle degeneration genetic disorder.

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