AstraZeneca Closes Amyloidosis Gap On Alnylam After Eplontersen Win
Positive Phase III For Ionis-Partnered Antisense Candidate
Executive Summary
AstraZeneca is preparing a US filing for hereditary transthyretin-mediated amyloid polyneuropathy for eplontersen, which it hopes will compete with Pfizer and Alnylam's therapies in that rare disease space.
You may also be interested in...
Alnylam’s Amvuttra To Take Off From Onpattro’s Runway
The company won approval in hATTR amyloidosis polyneuropathy for the RNAi drug, which offers quarterly subcutaneous dosing versus Onpattro’s I.V. administration every three weeks.
AstraZeneca’s Farxiga DELIVERs With Fresh Heart Failure Data
AstraZeneca's SGLT2 inhibitor Farxiga could soon get approval as an option for all heart failure patients following the success of the large Phase III DELIVER trial in people with preserved ejection fraction.
New Data Boost For Intellia’s Pioneering In Vivo Gene-Editing Therapy
New data show that a high dose of Intellia’s in vivo CRISPR-Cas9 based therapy is safe and effective for up to six months, which could unlock a new era in genetic disease treatment.