Biogen Seeking A Path Forward After Phase III Tofersen Study Fails In ALS
Ionis-Partnered Asset Developed For SOD1 Genetic Mutations
Executive Summary
The drug showed favorable but not significant trends across secondary endpoints, and greater efficacy in slower-progressing patients and those treated earlier in the disease, in a small subpopulation.
You may also be interested in...
Pharma Outlook 2022: What Next After A Year Of Innovation And Growth?
The biopharma industry broke records again in 2021 with the amount of money raised for drug development. After a year of rapid growth, what will 2022 bring for market dynamics and R&D catalysts in biopharma?
Well-Funded Chinese Venture Races To Clinic Amid Reviving CNS Interest
SciNeuro’s latest in-licensing deals include three assets for major neurodegenerative diseases from Lilly and Mabylon, but the Chinese bioventure is looking beyond the shopping spree at what it sees as outstanding CNS needs.
Amylyx Will Submit ALS Drug For Approval In The Coming Months
After discussions with the US FDA, the company determined it can file AMX0035 based on Phase II/III results and interim Phase III data. Amylyx is sticking with its go-it-alone strategy for global commercialization.