Idorsia's Fabry Drug Founders In Phase III
Lucerastat Fails To Reduce Neuropathic Pain
Executive Summary
The prospects of lucerastat becoming Idorsia's second drug to be filed with regulators, after the insomnia treatment daridorexant, look slim after a Phase III fail for the Fabry disease therapy.
You may also be interested in...
Idorsia’s Quviviq Needs To Rise And Shine After Slow Launch
The company’s Quviviq launch has fallen short of early expectations, but Idorsia believes a patient approach will pay off for the blockbuster-tipped insomnia treatment.
Sangamo's Fabry Gene Therapy May Be A STAAR In The Making
The US biotech has presented interesting preliminary data from the first four patients treated in the Phase I/II STAAR study evaluating isaralgagene civaparvovec for Fabry.
Chiesi's Commercial Hopes In US Hit By FDA Letter
Shares in Protalix sank more than 30% after the company received a complete response letter from US regulators for pegunigalsidase alfa for Fabry disease. No inspection of the company's manufacturing plant in Israel appears to be the main sticking point.