Sarepta Leapfrogs Pfizer In The US, Launching DMD Gene Therapy Pivotal Trial
The company has initiated the first pivotal double-blind gene therapy trial in DMD in the US in a tight race with Pfizer.
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Sarepta’s Exondys 51 Successor On Clinical Hold, But Quick Resolution Expected
The FDA placed a hold on the Phase II study of SRP-5051, which uses the company’s next-generation peptide conjugation technology, but Sarepta thinks it can address safety questions in short order.
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Quick Listen: Scrip’s Five Must-Know Things
In this week's podcast edition of Five Must-Know Things: will a new oral antiviral be transformative for COVID?; OX40 drugs gain prominence in atopic dermatitis; J&J adds pace to RSV vaccine race; Sarepta leapfrogs Pfizer in DMD gene therapy; and how real-world evidence and randomized trials might go together.