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AZ's Rare Disease Unit Reports Positive Phase III Results For Copper-Binding ALXN1840

Effective In Wilson Disease

Executive Summary

Alexion/AstraZeneca has announced positive top-line results from the Phase III study of ALXN1840 in patients with the rare genetic disorder, Wilson disease, including in patients already on standard-of-care therapies. The compound is ahead of two candidate gene therapies from other companies at early-stage clinical development.

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