ProQR Raises $90m To Advance Eye Disease Pipeline
Lead Candidates For LCA10 And Usher Syndrome
The Dutch biotech has firmed up its finances as its promising pipeline of RNA therapies for rare genetic eye disease starts to move through the clinic.
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ProQR Remains Confident In Pipeline After Sepofarsen Flop, Analysts Not So Much
The company is pinning hopes on its Usher syndrome and retinitis pigmentosa programs, but the disconnect between Phase I/II success and Phase II/III failure dented analysts’ enthusiasm.
First Results From Editas CRISPR Eye Therapy Underwhelm Investors
While rivals Intellia impressed with their first in vivo CRISPR gene-editing data, Editas’s first results in just two patients are not enough to convince investors.
Lilly To Try ProQR’s RNA-Editing Technology In Liver, Neurology Indications
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