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Orphazyme's Arimoclomol Disappoints For Muscle-Wasting Disorder

Pivotal Trial Failure For ‘Pipeline-In-A-Product’

Executive Summary

The Danish biotech's stock sank after arimoclomol failed in a Phase II/III trial for inclusion body myositis. Orphazyme is hoping for much better news in the coming weeks as the US FDA makes its decision on the drug as a treatment for Niemann-Pick disease Type C.

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