Roche’s Evrysdi Approved For SMA, Priced Below Competitors
Oral drug will rival Biogen, Novartis therapies
Executive Summary
Risdiplam’s efficacy across two clinical trials and oral dosing made it a credible threat before its US FDA approval, but its weight-based pricing falls below Biogen’s Spinraza and Novartis’s Zolgensma.
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Deal Snapshot: The deal, with an upfront payment of $45m, is the latest of several involving large biopharma companies and smaller firms focused on small molecule drugs based on RNA biology.
Biogen Acquires Ionis’ Spinal Muscular Atrophy Candidate As Spinraza Loses Its Shine
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Novartis Can Again Pursue Bigger Zolgensma Market After FDA Lifts OAV-101 Hold
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