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Genentech’s SMA Type 1 Data Strengthen Case Backing Risdiplam Approval

Executive Summary

With top-line data showing efficacy in type 1 SMA patients, risdiplam may be able to obtain a label that would address significantly more patients than Novartis’ Zolgensma. Final efficacy data will show how drug’s efficacy compares to Biogen’s Spinraza.

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