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Sangamo Data Is A Moment For Gene Editing, But Leaves Questions

Executive Summary

Sangamo announced the first human data for a gene editing treatment, SB-913 for MPS II, but the early data in just four patients shows gene editing technology has a long way to go before new medicines reach the market.

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Daily round-up of news and notes from the 2019 J.P. Morgan Healthcare Conference in San Francisco: AstraZeneca's net prices set to slide in 2019; biotechs ponder disasters from government shutdown; Denali moves into gene therapy; Sangamo clarifies partnering strategy; and Scrip talks to Allergan and Aptinyx about upcoming NMDA data releases.

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