Spark Therapeutics' Vision Loss Gene Therapy Heads For EU Market
A gene therapy for inherited retinal conditions leading to blindness could be marketed in Europe in 2018, but needs to avoid the setbacks dealt to UniQure’s gene therapy, Glybera, that is being withdrawn from the EU market.
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UniQure will not seek marketing authorization renewal for Glybera in the EU before it expires in October, but the company does not see the product's commercial failure as a sign that the market won't accept gene therapies or their high price tags.
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