Global Blood Therapeutics Inc.
Stopping the cycle of sickle cell disease
This article was originally published in Start Up
Executive Summary
Global Blood Therapeutic Inc.'s homegrown lead candidate is an oral, once-daily drug aimed at sickle cell disease, a genetic condition that causes red blood cells to become deformed or “sickled." The goal with GBT440 is to correct the disease, so that patients would actually have no evidence of it following treatment.
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