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Delayed Reaction: BioMarin Rises On Pegvaliase Data

This article was originally published in Scrip

Executive Summary

BioMarin Pharmaceutical Inc. has bounced back from a stock price slump that occurred after it reported that pegvaliase, the company's second therapy to treat phenylketonuria (PKU), met the primary endpoint in a Phase III clinical trial, but failed to meet a key secondary endpoint.

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