Kalydeco expanded in CF patients with R117H mutation
This article was originally published in Scrip
The FDA on 29 December gave Vertex Pharmaceuticals the go-ahead to expand the use of its cystic fibrosis drug Kalydeco (ivacaftor) in patients 6 years or older with the R117H mutation, even though the medicine failed a Phase III trial in that population.
You may also be interested in...
With new funding in hand, Moderna and its infectious disease venture Valera are going full-speed ahead with a Zika vaccine, taking an mRNA approach, which they said could be a more rapid strategy to try to stop the disease.
Allergan CEO Brent Saunders vows not to engage in price gouging and says his firm will limit cost increases to single-digit percentages, occurring only once per year. But it's unclear whether Saunders will stand as a lone wolf in the industry or if others will make similar pledges.
Hillary Clinton's plan to rein in high prices of older medicines, which includes creating a federal panel that has authority to impose fines, may grab headlines, but some analysts think it's unlikely to get very far in a divided Washington.