Raptor rises on US Procysbi OK
This article was originally published in Scrip
Raptor Pharmaceuticals gained the US FDA's OK on 30 April to market Procysbi (cysteamine bitartrate) as a therapy for adults and children as young as six years to manage nephropathic cystinosis, a rare, life-threatening metabolic lysosomal storage disorder that causes toxic accumulation of cystine in all cells, tissues, and organs in the body.
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