Non-profit group's support helps Repligen win Pfizer deal for SMA drug
This article was originally published in Scrip
Executive Summary
Repligen has made progress in its recent shift away from drug development to focus on bioprocessing by licensing its Phase I spinal muscular atrophy (SMA) program to Pfizer for up to $70 million plus royalties, in a deal that validates the more than $13 million invested by the non-profit group Families of SMA (FSMA) in the small molecule enzyme inhibitor RG3039.
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