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US FDA grants standard review for Raptor cystinosis treatment

This article was originally published in Scrip

Executive Summary

Investors cheered the US FDA's acceptance of Raptor Pharmaceutical's new drug application (NDA) for RP103 (cysteamine bitartrate delayed-release capsules) as a treatment for nephropathic cystinosis, a rare genetic lysosomal storage disorder, with shares of the Novato, California biotech rising as high as 7.4%.



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