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FDA panel recommends Recordati's carglumic acid for rare disease

This article was originally published in Scrip

Executive Summary

The US FDA's endocrinologic and metabolic drugs advisory committee on January 13 voted unanimously to recommend that the agency approve Recordati's carglumic acid for the treatment of hyperammonaemia due to the deficiency of the hepatic enzyme N-acetylglutamate synthase (NAGS).

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